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Q40277701-158D71CB-7CB1-4EA6-9189-5D615763E81F
Q40277701-158D71CB-7CB1-4EA6-9189-5D615763E81F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40277701-158D71CB-7CB1-4EA6-9189-5D615763E81F
Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.
P2860
Q40277701-158D71CB-7CB1-4EA6-9189-5D615763E81F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40277701-158D71CB-7CB1-4EA6-9189-5D615763E81F
rank
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Statement
wasDerivedFrom
34510a164eb193c0c62a5e4942d73b8a724b6303
P2860
Factor IX expression in skeletal muscle of a severe hemophilia B patient 10 years after AAV-mediated gene transfer.