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Q40277701-1E36DA47-8D22-4D68-9F69-1C1728075E52
Q40277701-1E36DA47-8D22-4D68-9F69-1C1728075E52
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http://www.wikidata.org/entity/statement/Q40277701-1E36DA47-8D22-4D68-9F69-1C1728075E52
Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.
P2860
Q40277701-1E36DA47-8D22-4D68-9F69-1C1728075E52
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40277701-1E36DA47-8D22-4D68-9F69-1C1728075E52
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wasDerivedFrom
34510a164eb193c0c62a5e4942d73b8a724b6303
P2860
Restoration of central nervous system alpha-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-associated viral type 2 vector delivery.