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Q40772336-FBD68D93-F097-4238-A507-2F0BAD673BF5
Q40772336-FBD68D93-F097-4238-A507-2F0BAD673BF5
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40772336-FBD68D93-F097-4238-A507-2F0BAD673BF5
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
P2860
Q40772336-FBD68D93-F097-4238-A507-2F0BAD673BF5
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40772336-FBD68D93-F097-4238-A507-2F0BAD673BF5
rank
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wasDerivedFrom
56bb2c764af339df6f6a3ab986889b707f606b1a
P2860
Correction of murine Rag2 severe combined immunodeficiency by lentiviral gene therapy using a codon-optimized RAG2 therapeutic transgene.