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Q41106058-140094A2-E921-4DFE-8474-5897F4DD977A
Q41106058-140094A2-E921-4DFE-8474-5897F4DD977A
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http://www.wikidata.org/entity/statement/Q41106058-140094A2-E921-4DFE-8474-5897F4DD977A
Short (16-mer) locked nucleic acid splice-switching oligonucleotides restore dystrophin production in Duchenne Muscular Dystrophy myotubes.
P2860
Q41106058-140094A2-E921-4DFE-8474-5897F4DD977A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41106058-140094A2-E921-4DFE-8474-5897F4DD977A
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5afd7da6fdaa591f3b2150973584d4cf5de54c49
P2860
Systemic administration of PRO051 in Duchenne's muscular dystrophy.