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Q41671484-290AE990-8859-41B2-A0EF-0031A7E7BEA2
Q41671484-290AE990-8859-41B2-A0EF-0031A7E7BEA2
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http://www.wikidata.org/entity/statement/Q41671484-290AE990-8859-41B2-A0EF-0031A7E7BEA2
An Exon-Specific U1snRNA Induces a Robust Factor IX Activity in Mice Expressing Multiple Human FIX Splicing Mutants.
P2860
Q41671484-290AE990-8859-41B2-A0EF-0031A7E7BEA2
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41671484-290AE990-8859-41B2-A0EF-0031A7E7BEA2
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wasDerivedFrom
1301f20b914a5d65fc94fb8a0cca5be73d8b4c43
P2860
Exon 45 skipping through U1-snRNA antisense molecules recovers the Dys-nNOS pathway and muscle differentiation in human DMD myoblasts.