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Q43268180-8E0BC40C-60F4-46AD-B87C-955EB3A77FAD
Q43268180-8E0BC40C-60F4-46AD-B87C-955EB3A77FAD
BestRank
Statement
http://www.wikidata.org/entity/statement/Q43268180-8E0BC40C-60F4-46AD-B87C-955EB3A77FAD
Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins.
P2860
Q43268180-8E0BC40C-60F4-46AD-B87C-955EB3A77FAD
BestRank
Statement
http://www.wikidata.org/entity/statement/Q43268180-8E0BC40C-60F4-46AD-B87C-955EB3A77FAD
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wasDerivedFrom
c54419300a37ea3a18db824b1d829ee7e007f52e
P2860
Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors.