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Q45861979-16041F64-46BC-4695-971D-B0CE36130919
Q45861979-16041F64-46BC-4695-971D-B0CE36130919
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45861979-16041F64-46BC-4695-971D-B0CE36130919
Efficient correction of Fabry mice and patient cells mediated by lentiviral transduction of hematopoietic stem/progenitor cells.
P2860
Q45861979-16041F64-46BC-4695-971D-B0CE36130919
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45861979-16041F64-46BC-4695-971D-B0CE36130919
rank
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wasDerivedFrom
175f79ca725ab44a417e184f3cec71ad9266611b
P2860
Fabry disease: preclinical studies demonstrate the effectiveness of alpha-galactosidase A replacement in enzyme-deficient mice.