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Q45865368-7F6892BD-85EB-47B1-B8C6-0C89D41637EC
Q45865368-7F6892BD-85EB-47B1-B8C6-0C89D41637EC
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Statement
http://www.wikidata.org/entity/statement/Q45865368-7F6892BD-85EB-47B1-B8C6-0C89D41637EC
Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice.
P2860
Q45865368-7F6892BD-85EB-47B1-B8C6-0C89D41637EC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45865368-7F6892BD-85EB-47B1-B8C6-0C89D41637EC
rank
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wasDerivedFrom
4968a4c6f27b8a5f749463dc36dc40623f61925e
P2860
Trans-splicing-mediated improvement in a severe mouse model of spinal muscular atrophy.