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Q45872078-AED3BAE2-41F3-4301-B7EF-D088DE164909
Q45872078-AED3BAE2-41F3-4301-B7EF-D088DE164909
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45872078-AED3BAE2-41F3-4301-B7EF-D088DE164909
How close are we to therapies for Sanfilippo disease?
P2860
Q45872078-AED3BAE2-41F3-4301-B7EF-D088DE164909
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45872078-AED3BAE2-41F3-4301-B7EF-D088DE164909
rank
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type
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Statement
wasDerivedFrom
5c29d55a7afe0afd5db5fafc64801d0d42a345e4
P2860
Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.