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Q47577667-A47933A6-0A4F-481F-BF13-452A45C20A37
Q47577667-A47933A6-0A4F-481F-BF13-452A45C20A37
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Statement
http://www.wikidata.org/entity/statement/Q47577667-A47933A6-0A4F-481F-BF13-452A45C20A37
A multicenter, retrospective medical record review of X-linked myotubular myopathy: The recensus study.
P2860
Q47577667-A47933A6-0A4F-481F-BF13-452A45C20A37
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47577667-A47933A6-0A4F-481F-BF13-452A45C20A37
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wasDerivedFrom
99b706b8edc0e63a5a42f320766ce4c2b73c9384
P2860
AAV-mediated intramuscular delivery of myotubularin corrects the myotubular myopathy phenotype in targeted murine muscle and suggests a function in plasma membrane homeostasis