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Q48507292-82593B2E-E68E-48F4-A673-06556017CE52
Q48507292-82593B2E-E68E-48F4-A673-06556017CE52
BestRank
Statement
http://www.wikidata.org/entity/statement/Q48507292-82593B2E-E68E-48F4-A673-06556017CE52
Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression.
P2860
Q48507292-82593B2E-E68E-48F4-A673-06556017CE52
BestRank
Statement
http://www.wikidata.org/entity/statement/Q48507292-82593B2E-E68E-48F4-A673-06556017CE52
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wasDerivedFrom
5e43ffce09022f159bb9cb8a2b9ad8dc607f4ae5
P2860
A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence