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Q48648024-4913C28F-802E-4283-92A4-7D49E33948EA
Q48648024-4913C28F-802E-4283-92A4-7D49E33948EA
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http://www.wikidata.org/entity/statement/Q48648024-4913C28F-802E-4283-92A4-7D49E33948EA
Use of antisense oligonucleotides to correct the splicing error in ISCU myopathy patient cell lines.
P2860
Q48648024-4913C28F-802E-4283-92A4-7D49E33948EA
BestRank
Statement
http://www.wikidata.org/entity/statement/Q48648024-4913C28F-802E-4283-92A4-7D49E33948EA
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8e3d4be4f8204fe4491df8729931a4df29383972
P2860
New developments in exon skipping and splice modulation therapies for neuromuscular diseases.