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1
Q50790826-3A90DC76-D6EA-4F86-9B6B-D52DB3DF035F
Q50790826-3A90DC76-D6EA-4F86-9B6B-D52DB3DF035F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q50790826-3A90DC76-D6EA-4F86-9B6B-D52DB3DF035F
Observational clinical study in juvenile-adult glycogenosis type 2 patients undergoing enzyme replacement therapy for up to 4 years.
P921
Q50790826-3A90DC76-D6EA-4F86-9B6B-D52DB3DF035F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q50790826-3A90DC76-D6EA-4F86-9B6B-D52DB3DF035F
rank
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type
BestRank
Statement
P921
Enzyme replacement therapy