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Q51734338-1F995D7A-56E3-436D-B4EB-23AF50386304
Q51734338-1F995D7A-56E3-436D-B4EB-23AF50386304
BestRank
Statement
http://www.wikidata.org/entity/statement/Q51734338-1F995D7A-56E3-436D-B4EB-23AF50386304
Reduction of lipid accumulation rescues Bietti's crystalline dystrophy phenotypes.
P2860
Q51734338-1F995D7A-56E3-436D-B4EB-23AF50386304
BestRank
Statement
http://www.wikidata.org/entity/statement/Q51734338-1F995D7A-56E3-436D-B4EB-23AF50386304
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wasDerivedFrom
669f1ffd042261b25a8b7c4013985cf42539fea9
P2860
Novel oral treatment of Gaucher's disease with N-butyldeoxynojirimycin (OGT 918) to decrease substrate biosynthesis.