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Q58577259-EBEF4AF1-FA4A-4346-A6C7-1C4B61D8FF49
Q58577259-EBEF4AF1-FA4A-4346-A6C7-1C4B61D8FF49
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58577259-EBEF4AF1-FA4A-4346-A6C7-1C4B61D8FF49
Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD
P2860
Q58577259-EBEF4AF1-FA4A-4346-A6C7-1C4B61D8FF49
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58577259-EBEF4AF1-FA4A-4346-A6C7-1C4B61D8FF49
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wasDerivedFrom
f480922db5737f5730f71dc3b2e038b49f16c01a
P2860
Severe toxicity in nonhuman primates and piglets following high-dose intravenous administration of an AAV vector expressing human SMN.