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Q58794894-AC49D6E8-B604-47FB-B8B3-E32DEBF6DD0B
Q58794894-AC49D6E8-B604-47FB-B8B3-E32DEBF6DD0B
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http://www.wikidata.org/entity/statement/Q58794894-AC49D6E8-B604-47FB-B8B3-E32DEBF6DD0B
Glucosylceramide synthase inhibition with lucerastat lowers globotriaosylceramide and lysosome staining in cultured fibroblasts from Fabry patients with different mutation types
P2860
Q58794894-AC49D6E8-B604-47FB-B8B3-E32DEBF6DD0B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58794894-AC49D6E8-B604-47FB-B8B3-E32DEBF6DD0B
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d5465f428864e6913b7c65bd8982d83ee6455305
P2860
Pharmacological chaperone therapy by active-site-specific chaperones in Fabry disease: in vitro and preclinical studies.