Wolman Disease [clinicaltrials_resource:2dd48abe9ffa18c35c1a4556da5c95fd]
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation [clinicaltrials:NCT00005900]clinicaltrials:NCT00176904clinicaltrials:NCT00383448A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype [clinicaltrials:NCT01358370]Trial in Children With Growth Failure Due to Early Onset Lysosomal Acid Lipase (LAL) Deficiency/Wolman Disease [clinicaltrials:NCT01371825]Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102 [clinicaltrials:NCT01473875]clinicaltrials:NCT01586455Lysosomal Acid Lipase (LAL) Deficiency Registry [clinicaltrials:NCT01633489]clinicaltrials:NCT01884220clinicaltrials:NCT02383641
condition [clinicaltrials_vocabulary:condition]
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation [clinicaltrials:NCT00005900]clinicaltrials:NCT00176904clinicaltrials:NCT00383448clinicaltrials:NCT00668564Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01307098]A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype [clinicaltrials:NCT01358370]Trial in Children With Growth Failure Due to Early Onset Lysosomal Acid Lipase (LAL) Deficiency/Wolman Disease [clinicaltrials:NCT01371825]Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102 [clinicaltrials:NCT01473875]Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of SBC-102 (Sebelipase Alfa) in Adult Subjects With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01488097]An Observational Study of Patients With Lysosomal Acid Lipase Deficiency/Cholesteryl Ester Storage Disease Phenotype [clinicaltrials:NCT01528917]clinicaltrials:NCT01586455Lysosomal Acid Lipase (LAL) Deficiency Registry [clinicaltrials:NCT01633489]Identification of Undiagnosed Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01716728]A Multicenter Study of SBC-102 (Sebelipase Alfa) in Patients With Lysosomal Acid Lipase Deficiency/ ARISE (Acid Lipase Replacement Investigating Safety and Efficacy) [clinicaltrials:NCT01757184]Novel Association of Cholesterol Ester Storage Disease Due to Lysosomal Acid Lipase Deficiency and Non-Alcoholic Fatty Liver Disease: A Prospective Clinical Study [clinicaltrials:NCT01791452]clinicaltrials:NCT01884220Safety and Efficacy Study of Sebelipase Alfa in Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT02112994]clinicaltrials:NCT02193867A Study to Identify and Characterize LAL-D Patients in High-risk Populations [clinicaltrials:NCT02345421]clinicaltrials:NCT02372513An Expanded Access Protocol for Sebelipase Alfa for Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT02376751]clinicaltrials:NCT02383641
condition browse [clinicaltrials_vocabulary:condition-browse]
Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation [clinicaltrials:NCT00005900]clinicaltrials:NCT00176904clinicaltrials:NCT00383448clinicaltrials:NCT00668564Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01307098]A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype [clinicaltrials:NCT01358370]Trial in Children With Growth Failure Due to Early Onset Lysosomal Acid Lipase (LAL) Deficiency/Wolman Disease [clinicaltrials:NCT01371825]Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102 [clinicaltrials:NCT01473875]Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of SBC-102 (Sebelipase Alfa) in Adult Subjects With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01488097]An Observational Study of Patients With Lysosomal Acid Lipase Deficiency/Cholesteryl Ester Storage Disease Phenotype [clinicaltrials:NCT01528917]clinicaltrials:NCT01586455Lysosomal Acid Lipase (LAL) Deficiency Registry [clinicaltrials:NCT01633489]Identification of Undiagnosed Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT01716728]A Multicenter Study of SBC-102 (Sebelipase Alfa) in Patients With Lysosomal Acid Lipase Deficiency/ ARISE (Acid Lipase Replacement Investigating Safety and Efficacy) [clinicaltrials:NCT01757184]Novel Association of Cholesterol Ester Storage Disease Due to Lysosomal Acid Lipase Deficiency and Non-Alcoholic Fatty Liver Disease: A Prospective Clinical Study [clinicaltrials:NCT01791452]clinicaltrials:NCT01884220Safety and Efficacy Study of Sebelipase Alfa in Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT02112994]clinicaltrials:NCT02193867A Study to Identify and Characterize LAL-D Patients in High-risk Populations [clinicaltrials:NCT02345421]clinicaltrials:NCT02372513An Expanded Access Protocol for Sebelipase Alfa for Patients With Lysosomal Acid Lipase Deficiency [clinicaltrials:NCT02376751]clinicaltrials:NCT02383641
condition mesh [clinicaltrials_vocabulary:condition-mesh]
Wolman Disease [clinicaltrials_resource:2dd48abe9ffa18c35c1a4556da5c95fd]
Bio2RDF identifier
2dd48abe9ffa18c35c1a4556da5c95fd
Bio2RDF namespace
clinicaltrials_resource
Bio2RDF uri
http://bio2rdf.org/clinicaltrials_resource:2dd48abe9ffa18c35c1a4556da5c95fd
identifier
clinicaltrials_resource:2dd48abe9ffa18c35c1a4556da5c95fd
title
Wolman Disease
@en
type
label
Wolman Disease [clinicaltrials_resource:2dd48abe9ffa18c35c1a4556da5c95fd]
@en
Wolman Disease