Survival at one year and the proportion of patients in need of ventilator support by one year one year [clinicaltrials_resource:43e07d9465f64592e228a125b8d5e53d]

Weekly infusion of laronidase enzyme replacement therapy followed by hematopoietic stem cell transplant.

Survival at one year and the proportion of patients in need of ventilator support by one year one year [clinicaltrials_resource:43e07d9465f64592e228a125b8d5e53d]

Weekly infusion of laronidase enzyme replacement therapy followed by hematopoietic stem cell transplant.