survival minimum of 1 year [clinicaltrials_resource:4b112e9291d2f345f8bbe1b8bc461e81]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan

survival minimum of 1 year [clinicaltrials_resource:4b112e9291d2f345f8bbe1b8bc461e81]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan