survival minimum of 1 year [clinicaltrials_resource:8dabc866a9460738246acffd63e351a1]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan

survival minimum of 1 year [clinicaltrials_resource:8dabc866a9460738246acffd63e351a1]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan