survival minimum of 1 year [clinicaltrials_resource:b4931ea9a538aba2794d4a73db826f15]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan

survival minimum of 1 year [clinicaltrials_resource:b4931ea9a538aba2794d4a73db826f15]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan