survival minimum of 1 year [clinicaltrials_resource:be907c70124aa9c5089db1f8dabddcc2]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan

survival minimum of 1 year [clinicaltrials_resource:be907c70124aa9c5089db1f8dabddcc2]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan