survival minimum of 1 year [clinicaltrials_resource:d1b8b54a6044094f76c1d975b11f2e30]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan

survival minimum of 1 year [clinicaltrials_resource:d1b8b54a6044094f76c1d975b11f2e30]

infusion of autologous CD34+ cells transduced with retroviral vector encoding ADA after non-myeloablative conditioning with Busulphan