Recommendations for the use of eliglustat in the treatment of adults with Gaucher disease type 1 in the United States
about
Rethinking fatigue in Gaucher diseaseThrombocytopenia and GBA gene mutation in a patient with adult type 1 Gaucher disease.Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.Gene therapy for lysosomal storage disorders: a good start.A new framework for evaluating the health impacts of treatment for Gaucher disease type 1.Progress and potential of non-inhibitory small molecule chaperones for the treatment of Gaucher disease and its implications for Parkinson disease.Personalized medicine: Genetic risk prediction of drug response.Gaucher disease: Progress and ongoing challenges.
P2860
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P2860
Recommendations for the use of eliglustat in the treatment of adults with Gaucher disease type 1 in the United States
description
2016 nî lūn-bûn
@nan
2016 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2016 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
name
Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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Recommendations for the use of ...... se type 1 in the United States
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P2093
P3181
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Recommendations for the use of ...... se type 1 in the United States
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P2093
Jeremy Ruskin
Joel Charrow
Manisha Balwani
Neal Weinreb
Ozlem Goker-Alpan
Paige Kaplan
Pramod Mistry
Priya S Kishnani
Thomas Andrew Burrow
P304
P3181
P356
10.1016/J.YMGME.2015.09.002
P407
P577
2016-02-01T00:00:00Z