Access to Orphan Drugs: A Comprehensive Review of Legislations, Regulations and Policies in 35 Countries
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Profitability and Market Value of Orphan Drug Companies: A Retrospective, Propensity-Matched Case-Control StudyDeterminants of orphan drugs prices in France: a regression analysis.A comparative study of orphan drug prices in Europe.Do payers value rarity? An analysis of the relationship between disease rarity and orphan drug prices in Europe.Analysis of cystic fibrosis-associated P67L CFTR illustrates barriers to personalized therapeutics for orphan diseasesEconomic Evaluation in Duchenne Muscular Dystrophy: Model Frameworks for Cost-Effectiveness Analysis.Recommendations from the European Working Group for Value Assessment and Funding Processes in Rare Diseases (ORPH-VAL).Review of 11 national policies for rare diseases in the context of key patient needs.Orphan medicinal products in Europe and United States to cover needs of patients with rare diseases: an increased common effort is to be foreseenThe need for a next-generation public health response to rare diseases.Accelerating Patients' Access to Advanced Therapies in the EU.Proposed changes to the reimbursement of pharmaceuticals and medical devices in Poland and their impact on market access and the pharmaceutical industry.The perverse impact of external reference pricing (ERP): a comparison of orphan drugs affordability in 12 European countries. A call for policy change.High yield process for the production of active human α-galactosidase a in CHO-K1 cells through lentivirus transgenesis.Treatable inherited rare movement disorders.Orphan drug policies and use in pediatric nephrology.Orphan drugs: Indian perspective.We need a "made in Canada" orphan drug framework.Multi-Criteria Decision Analysis (MCDA) Models in Health Technology Assessment of Orphan Drugs-a Systematic Literature Review. Next Steps in Methodology Development?Disease and economic burden for rare diseases in Taiwan: A longitudinal study using Taiwan's National Health Insurance Research Database
P2860
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P2860
Access to Orphan Drugs: A Comprehensive Review of Legislations, Regulations and Policies in 35 Countries
description
2015 nî lūn-bûn
@nan
2015 թուականին հրատարակուած գիտական յօդուած
@hyw
2015 թվականին հրատարակված գիտական հոդված
@hy
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@ast
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
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Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
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type
label
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@ast
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@en
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
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Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@ast
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@en
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@nl
P2093
P2860
P3181
P1433
P1476
Access to Orphan Drugs: A Comp ...... s and Policies in 35 Countries
@en
P2093
Christine Y Lu
Todd Gammie
Zaheer Ud-Din Babar
P2860
P304
P3181
P356
10.1371/JOURNAL.PONE.0140002
P407
P577
2015-01-01T00:00:00Z