24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
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204th ENMC International Workshop on Biomarkers in Duchenne Muscular Dystrophy 24-26 January 2014, Naarden, The NetherlandsThe burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence reviewLong term natural history data in ambulant boys with Duchenne muscular dystrophy: 36-month changes.Six-minute walk test: reference values and prediction equation in healthy boys aged 5 to 12 years.Long-Term Efficacy, Safety, and Pharmacokinetics of Drisapersen in Duchenne Muscular Dystrophy: Results from an Open-Label Extension StudyAffinity proteomics within rare diseases: a BIO-NMD study for blood biomarkers of muscular dystrophiesPharmacologic management of Duchenne muscular dystrophy: target identification and preclinical trialsAtaluren treatment of patients with nonsense mutation dystrophinopathy.Age-related longitudinal changes in metabolic energy expenditure during walking in boys with Duchenne muscular dystrophy.The 6 minute walk test and performance of upper limb in ambulant duchenne muscular dystrophy boysTimed Rise from Floor as a Predictor of Disease Progression in Duchenne Muscular Dystrophy: An Observational Study.Muscle Activation during Gait in Children with Duchenne Muscular Dystrophy.Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics.The NorthStar Ambulatory Assessment in Duchenne muscular dystrophy: considerations for the design of clinical trials.DMD genotypes and loss of ambulation in the CINRG Duchenne Natural History Study.Circulating Biomarkers for Duchenne Muscular Dystrophy.Ongoing therapeutic trials and outcome measures for Duchenne muscular dystrophy.Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy.Longitudinal community walking activity in Duchenne muscular dystrophy.Developing a Natural History Progression Model for Duchenne Muscular Dystrophy Using the Six-Minute Walk Test.Exon skipping: a first in class strategy for Duchenne muscular dystrophy.Electrical impedance myography for assessment of Duchenne muscular dystrophy.Health-related quality of life and functional changes in DMD: A 12-month longitudinal cohort study.Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy.Functional changes in Becker muscular dystrophy: implications for clinical trials in dystrophinopathiesCategorizing natural history trajectories of ambulatory function measured by the 6-minute walk distance in patients with Duchenne muscular dystrophy.Spinal muscular atrophy functional composite score: A functional measure in spinal muscular atrophy.6 Minute walk test in Duchenne MD patients with different mutations: 12 month changes.Seeking a better landscape for therapy development in neuromuscular disorders.Duchenne and Becker Muscular Dystrophies: A Review of Animal Models, Clinical End Points, and Biomarker Quantification.Boys With Duchenne Muscular Dystrophy: 1-Year Locomotor Changes in Relation to a Control Group.Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management.Relationship between muscle strength and motor function in Duchenne muscular dystrophy.Fibronectin is a serum biomarker for Duchenne muscular dystrophy
P2860
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P2860
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
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2013年の論文
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name
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@ast
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
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type
label
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@ast
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@en
prefLabel
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@ast
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@en
P2093
P2860
P50
P3181
P1433
P1476
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy
@en
P2093
Antonella Pini
Claudio Bruno
Elena Pegoraro
Elena Stacy Mazzone
Emanuela Viggiano
Enrica Rolle
Filippo Cavallaro
Flaviana Bianco
Francesca Rossi
Gianluca Vita
P2860
P304
P3181
P356
10.1371/JOURNAL.PONE.0052512
P407
P50
P577
2013-01-01T00:00:00Z