Similar therapeutic efficacy between a single administration of gene therapy and multiple administrations of recombinant enzyme in a mouse model of lysosomal storage disease
about
Gene therapy for lysosomal storage disorders: a good start.Prevalence of anti-adeno-associated virus serotype 8 neutralizing antibodies and arylsulfatase B cross-reactive immunologic material in mucopolysaccharidosis VI patient candidates for a gene therapy trial.Recombinant adeno-associated virus vectors in the treatment of rare diseases.Low-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease.Lysosomal enzyme replacement therapies: Historical development, clinical outcomes, and future perspectives.Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI.Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression.
P2860
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P2860
Similar therapeutic efficacy between a single administration of gene therapy and multiple administrations of recombinant enzyme in a mouse model of lysosomal storage disease
description
2014 nî lūn-bûn
@nan
2014 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@ast
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@en
type
label
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@ast
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@en
prefLabel
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@ast
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@en
P2093
P2860
P356
P1433
P1476
Similar therapeutic efficacy b ...... l of lysosomal storage disease
@en
P2093
Elvira De Leonibus
Gabriella Cotugno
Pamela Claudiani
Paola Saccone
Rita Ferla
P2860
P304
P356
10.1089/HUM.2013.213
P577
2014-04-11T00:00:00Z