CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
about
P1343
KLHL41 stabilizes skeletal muscle sarcomeres by nonproteolytic ubiquitination.Functional correction of dystrophin actin binding domain mutations by genome editing.Gene Editing and Human Pluripotent Stem Cells: Tools for Advancing Diabetes Disease Modeling and Beta-Cell Development.Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.The Conspicuity of CRISPR-Cpf1 System as a Significant Breakthrough in Genome Editing.Gene activation in human cells using CRISPR/Cpf1-p300 and CRISPR/Cpf1-SunTag systems.Class 2 CRISPR-Cas RNA-guided endonucleases: Swiss Army knives of genome editing.Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing.Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype.Short telomeres - A hallmark of heritable cardiomyopathies.A New Kid on the Playground of CRISPR DMD Therapy.Gene Editing and Gene-Based Therapeutics for Cardiomyopathies.Innovative Therapeutic Strategies for Cystic Fibrosis: Moving Forward to CRISPR Technique.Genetic editing and interrogation with Cpf1 and caged truncated pre-tRNA-like crRNA in mammalian cells.Class 2 CRISPR/Cas: an expanding biotechnology toolbox for and beyond genome editingTherapeutic approaches for cardiac regeneration and repair
P2860
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P2860
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
description
2017 nî lūn-bûn
@nan
2017 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2017 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2017年の論文
@ja
2017年学术文章
@wuu
2017年学术文章
@zh-cn
2017年学术文章
@zh-hans
2017年学术文章
@zh-my
2017年学术文章
@zh-sg
2017年學術文章
@yue
name
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@ast
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@en
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@nl
type
label
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@ast
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@en
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@nl
prefLabel
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@ast
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@en
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
@nl
P2093
P2860
P50
P356
P1433
P1476
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice
@en
P2093
Chengzu Long
Eric N Olson
John R McAnally
Rhonda Bassel-Duby
P2860
P304
P356
10.1126/SCIADV.1602814
P4510
P577
2017-04-12T00:00:00Z