Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
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Enzyme replacement therapy with galsulfase for mucopolysaccharidosis type VIEnzyme replacement therapy with galsulfase for mucopolysaccharidosis type VIRespiratory and sleep disorders in mucopolysaccharidosisClinical overview and treatment options for non-skeletal manifestations of mucopolysaccharidosis type IVAManagement of Life-Threatening Tracheal Stenosis and Tracheomalacia in Patients with MucopolysaccharidosesMucopolysaccharidosis VI.Long-term cognitive follow-up in children treated for Maroteaux-Lamy syndrome.Ethical and economic considerations of rare diseases in ethnic minorities: the case of mucopolysaccharidosis VI in Colombia.Enzyme replacement therapy for mucopolysaccharidosis VI: long-term cardiac effects of galsulfase (Naglazyme®) therapyMucopolysaccharidosis type VI phenotypes-genotypes and antibody response to galsulfase.Reduced Arylsulfatase B activity in leukocytes from cystic fibrosis patientsLong-term galsulfase enzyme replacement therapy in Taiwanese mucopolysaccharidosis VI patients: A case seriesHaploidentical stem cell transplantation in two children with mucopolysaccharidosis VI: clinical and biochemical outcome.Impact of long-term elosulfase alfa treatment on respiratory function in patients with Morquio A syndrome.Diagnosis of the mucopolysaccharidoses.Therapy for the mucopolysaccharidoses.Current and potential therapeutic strategies for mucopolysaccharidoses.Clinical Evolution After Enzyme Replacement Therapy in Twins with the Severe Form of Maroteaux-Lamy SyndromeMucopolysaccharidosis VI: cardiac involvement and the impact of enzyme replacement therapy.Design, baseline characteristics, and early findings of the MPS VI (mucopolysaccharidosis VI) Clinical Surveillance Program (CSP).Clinical characteristics of adults with slowly progressing mucopolysaccharidosis VI: a case series.Natural history and galsulfase treatment in mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrome)--10-year follow-up of patients who previously participated in an MPS VI Survey Study.Enzyme replacement therapy improves joint motion and outcome of the 12-min walk test in a mucopolysaccharidosis type VI patient previously treated with bone marrow transplantation.
P2860
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P2860
Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
description
2010 nî lūn-bûn
@nan
2010 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@ast
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@en
type
label
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@ast
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@en
prefLabel
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@ast
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@en
P2093
P2860
P1476
Enzyme replacement therapy for ...... cetylgalactosamine 4-sulfatase
@en
P2093
Barbara Plecko
Celeste Decker
Chester B Whitley
David Ketteridge
Elisa Leão Teles
Ida Vanessa D Schwartz
J Edmond Wraith
John J Hopwood
Karen Hardy
Laila Arash
P2860
P2888
P356
10.1007/S10545-009-9007-8
P577
2010-02-06T00:00:00Z
P5875
P6179
1042928055