Clinical applications of gene therapy for primary immunodeficiencies.
about
Clinical development of gene therapy: results and lessons from recent successesTowards in vivo amplification: Overcoming hurdles in the use of hematopoietic stem cells in transplantation and gene therapyAdvances in the Care of Primary Immunodeficiencies (PIDs): from Birth to Adulthood.Functional Restoration of gp91phox-Oxidase Activity by BAC Transgenesis and Gene Targeting in X-linked Chronic Granulomatous Disease iPSCs.In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution PhasesLong-Term Safety Follow-Up of Subjects Previously Treated with Non-Replicating Retroviral Vector-Based Gene Therapies.Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency.Prolonged Integration Site Selection of a Lentiviral Vector in the Genome of Human Keratinocytes.Gene therapy research in Asia.Virus-Like Particles Derived from HIV-1 for Delivery of Nuclear Proteins: Improvement of Production and Activity by Protein Engineering.Hematopoietic Stem Cell Transplantation for Primary Immune Deficiency Disorders.Recent advances in RNAi-based strategies for therapy and prevention of HIV-1/AIDS.Current status of ex vivo gene therapy for hematological disorders: a review of clinical trials in Japan around the world.Pseudotyping of lentiviral vector with novel vesiculovirus envelope glycoproteins derived from Chandipura and Piry viruses.Genome Editing Techniques and Their Therapeutic Applications.Genetic Engineering and Manufacturing of Hematopoietic Stem Cells.Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I.A novel common gamma chain mutation in a Chinese family with X-linked severe combined immunodeficiency (X-SCID; T(-)NK(-)B(+)).Engineering Next-Generation BET-Independent MLV Vectors for Safer Gene Therapy.Targeting expression to megakaryocytes and platelets by lineage-specific lentiviral vectors.Clinical development of CAR T cells-challenges and opportunities in translating innovative treatment conceptsMultiparametric Whole Blood Dissection: A one-shot comprehensive picture of the human hematopoietic system.Loop-mediated isothermal amplification (LAMP) as an alternative to PCR: A rapid on-site detection of gene doping.High Efficiency Gene Correction in Hematopoietic Cells by Donor-Template-Free CRISPR/Cas9 Genome Editing.NADPH Oxidase Deficiency: A Multisystem Approach.A comparison of intrauterine hemopoietic cell transplantation and lentiviral gene transfer for the correction of severe β-thalassemia in a HbbTh3/+ murine model.
P2860
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P2860
Clinical applications of gene therapy for primary immunodeficiencies.
description
2015 nî lūn-bûn
@nan
2015 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2015 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Clinical applications of gene therapy for primary immunodeficiencies.
@ast
Clinical applications of gene therapy for primary immunodeficiencies.
@en
type
label
Clinical applications of gene therapy for primary immunodeficiencies.
@ast
Clinical applications of gene therapy for primary immunodeficiencies.
@en
prefLabel
Clinical applications of gene therapy for primary immunodeficiencies.
@ast
Clinical applications of gene therapy for primary immunodeficiencies.
@en
P2860
P356
P1433
P1476
Clinical applications of gene therapy for primary immunodeficiencies.
@en
P2093
Maria Pia Cicalese
P2860
P304
P356
10.1089/HUM.2015.047
P577
2015-04-01T00:00:00Z