Site-specific genome editing for correction of induced pluripotent stem cells derived from dominant dystrophic epidermolysis bullosa.
about
Raising Awareness Among Healthcare Providers about Epidermolysis Bullosa and Advancing Toward a Cure.COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa.Next generation human skin constructs as advanced tools for drug development.Gene editing for skin diseases: designer nucleases as tools for gene therapy of skin fragility disorders.What rheumatologists need to know about CRISPR/Cas9.CRISPR Genome Engineering for Human Pluripotent Stem Cell Research.Ex vivo and in vivo genome editing: a regulatory scientific framework from early development to clinical implementation.Report of the 13th Annual International Pachyonychia Congenita Consortium Symposium.An efficient platform for generating somatic point mutations with germline transmission in the zebrafish by CRISPR/Cas9-mediated gene editing.Deletion of a Pathogenic Mutation-Containing Exon of COL7A1 Allows Clonal Gene Editing Correction of RDEB Patient Epidermal Stem Cells.CRISPR therapeutic tools for complex genetic disorders and cancer (Review).Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed Repair
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P2860
Site-specific genome editing for correction of induced pluripotent stem cells derived from dominant dystrophic epidermolysis bullosa.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Site-specific genome editing f ...... trophic epidermolysis bullosa.
@en
type
label
Site-specific genome editing f ...... trophic epidermolysis bullosa.
@en
prefLabel
Site-specific genome editing f ...... trophic epidermolysis bullosa.
@en
P2093
P2860
P356
P1476
Site-specific genome editing f ...... trophic epidermolysis bullosa.
@en
P2093
Angela M Christiano
Satoru Shinkuma
Zongyou Guo
P2860
P304
P356
10.1073/PNAS.1512028113
P407
P577
2016-05-03T00:00:00Z