Receptor-mediated delivery of engineered nucleases for genome modification.
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Enabling functional genomics with genome engineeringCell-penetrating peptide-mediated delivery of TALEN proteins via bioconjugation for genome engineeringEfficient Recreation of t(11;22) EWSR1-FLI1+ in Human Stem Cells Using CRISPR/Cas9.Engineering synthetic TALE and CRISPR/Cas9 transcription factors for regulating gene expressionNew type of BACE1 siRNA delivery to cells.Improved cell-penetrating zinc-finger nuclease proteins for precision genome engineeringOvercoming the challenges in administering biopharmaceuticals: formulation and delivery strategies.Controlled delivery of β-globin-targeting TALENs and CRISPR/Cas9 into mammalian cells for genome editing using microinjectionMultistage vector (MSV) therapeutics.Targeted genome editing by lentiviral protein transduction of zinc-finger and TAL-effector nucleasesA guide to genome engineering with programmable nucleases.Emerging gene editing strategies for Duchenne muscular dystrophy targeting stem cells.Precision genome editing: a small revolution for glycobiology.Recent developments and clinical studies utilizing engineered zinc finger nuclease technology.Efficient delivery of nuclease proteins for genome editing in human stem cells and primary cells.Cell-penetrating peptides and their utility in genome function modifications (Review).Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell Type Specific Gene Editing.
P2860
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P2860
Receptor-mediated delivery of engineered nucleases for genome modification.
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 16 August 2013
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Receptor-mediated delivery of engineered nucleases for genome modification.
@en
Receptor-mediated delivery of engineered nucleases for genome modification.
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type
label
Receptor-mediated delivery of engineered nucleases for genome modification.
@en
Receptor-mediated delivery of engineered nucleases for genome modification.
@nl
prefLabel
Receptor-mediated delivery of engineered nucleases for genome modification.
@en
Receptor-mediated delivery of engineered nucleases for genome modification.
@nl
P2093
P2860
P356
P1476
Receptor-mediated delivery of engineered nucleases for genome modification.
@en
P2093
David L Spector
Davies G Agyekum
Haiyan Xiao
Lahcen Jaafar
Marlene F Wade
Matthew H Porteus
R Ileng Kumaran
Steffen E Meiler
William S Dynan
P2860
P356
10.1093/NAR/GKT710
P407
P577
2013-08-16T00:00:00Z