Systemic delivery of factor IX messenger RNA for protein replacement therapy
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Advances in the delivery of RNA therapeutics: from concept to clinical reality.mRNA mediates passive vaccination against infectious agents, toxins, and tumors.Targeted mRNA Therapy for Ornithine Transcarbamylase Deficiency.mRNA treatment produces sustained expression of enzymatically active human ADAMTS13 in mice.Tools for translation: non-viral materials for therapeutic mRNA delivery
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Systemic delivery of factor IX messenger RNA for protein replacement therapy
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 15 February 2017
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Systemic delivery of factor IX messenger RNA for protein replacement therapy
@en
Systemic delivery of factor IX messenger RNA for protein replacement therapy.
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type
label
Systemic delivery of factor IX messenger RNA for protein replacement therapy
@en
Systemic delivery of factor IX messenger RNA for protein replacement therapy.
@nl
prefLabel
Systemic delivery of factor IX messenger RNA for protein replacement therapy
@en
Systemic delivery of factor IX messenger RNA for protein replacement therapy.
@nl
P2093
P2860
P356
P1476
Systemic delivery of factor IX messenger RNA for protein replacement therapy
@en
P2093
Inder M Verma
Jerel B Vega
Kiyoshi Tachikawa
Nina Tonnu
Pad Chivukula
Pattraranee Limphong
Priya P Karmali
Suvasini Ramaswamy
P2860
P304
E1941-E1950
P356
10.1073/PNAS.1619653114
P407
P577
2017-02-15T00:00:00Z