Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency
about
Advances of gene therapy for primary immunodeficienciesHematopoietic cell transplantation for hemophagocytic lymphohistiocytosis: recent advances and controversiesGene therapy for primary immune deficiencies: a Canadian perspective.Gene therapy for monogenic disorders of the bone marrow.Stem cell transplantation for the treatment of immunodeficiency in children: current status and hopes for the future.High Level of Perforin Expression Is Required for Effective Correction of Hemophagocytic Lymphohistiocytosis.Evolving Gene Therapy in Primary Immunodeficiency.T cell gene therapy for perforin deficiency corrects cytotoxicity defects and prevents Haemophagocytic Lymphohistiocytosis manifestations.
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P2860
Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency
description
2014 nî lūn-bûn
@nan
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
2014年论文
@zh
2014年论文
@zh-cn
name
Perforin gene transfer into he ...... models of perforin deficiency
@en
Perforin gene transfer into he ...... models of perforin deficiency.
@nl
type
label
Perforin gene transfer into he ...... models of perforin deficiency
@en
Perforin gene transfer into he ...... models of perforin deficiency.
@nl
prefLabel
Perforin gene transfer into he ...... models of perforin deficiency
@en
Perforin gene transfer into he ...... models of perforin deficiency.
@nl
P2093
P2860
P50
P356
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Perforin gene transfer into he ...... models of perforin deficiency
@en
P2093
Adrianne E Hontz
Christopher Baum
Claudia A Montiel-Equihua
H Bobby Gaspar
Maria E Alonso-Ferrero
Marlene Carmo
Michael B Jordan
Michael P Blundell
Paritha Arumugam
Punam Malik
P2860
P304
P356
10.1038/MT.2014.242
P577
2014-12-19T00:00:00Z