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1
Q39172747-8E8B3B24-5EAE-40F0-ACC7-5C65C37CD2FF
Q39172747-8E8B3B24-5EAE-40F0-ACC7-5C65C37CD2FF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39172747-8E8B3B24-5EAE-40F0-ACC7-5C65C37CD2FF
Targeting CPS1 in the treatment of Carbamoyl phosphate synthetase 1 (CPS1) deficiency, a urea cycle disorder.
P50
Q39172747-8E8B3B24-5EAE-40F0-ACC7-5C65C37CD2FF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39172747-8E8B3B24-5EAE-40F0-ACC7-5C65C37CD2FF
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
64fe0ec55af1860737c2cd59aa8584d9b7b08c52
P1545
2
http://www.w3.org/2001/XMLSchema#string
P50
Johannes Häberle