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Q53610521-389ADA3B-5CA8-4435-A583-A2136A3789F3
Q53610521-389ADA3B-5CA8-4435-A583-A2136A3789F3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q53610521-389ADA3B-5CA8-4435-A583-A2136A3789F3
Temporary Efficacy of Pyrimethamine in Juvenile-Onset Tay-Sachs Disease Caused by 2 Unreported HEXA Mutations in the Indian Population.
P2860
Q53610521-389ADA3B-5CA8-4435-A583-A2136A3789F3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q53610521-389ADA3B-5CA8-4435-A583-A2136A3789F3
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
fda7f568b67d96dc3d178ac786a19778620c94c1
P2860
Pharmacological Chaperone Therapy: Preclinical Development, Clinical Translation, and Prospects for the Treatment of Lysosomal Storage Disorders.