about
Increased fluid secretion after adenoviral-mediated transfer of the human aquaporin-1 cDNA to irradiated miniature pig parotid glandsGene targeting of mutant COL1A2 alleles in mesenchymal stem cells from individuals with osteogenesis imperfectaGOLGA2/GM130, cis-Golgi matrix protein, is a novel target of anticancer gene therapyThunder and lightning: immunotherapy and oncolytic viruses collideTherapeutic potential of intracerebroventricular replacement of modified human β-hexosaminidase B for GM2 gangliosidosisTargeting improves MSC treatment of inflammatory bowel diseaseRecombinant Newcastle disease virus as a vaccine vector for cancer therapyVEGF blockade enables oncolytic cancer virotherapy in part by modulating intratumoral myeloid cellsAAV-mediated liver-specific MPV17 expression restores mtDNA levels and prevents diet-induced liver failureTumor-specific expression of microRNA-26a suppresses human hepatocellular carcinoma growth via cyclin-dependent and -independent pathwaysPhase I trial of "bi-shRNAi(furin)/GMCSF DNA/autologous tumor cell" vaccine (FANG) in advanced cancerSelf-complementary AAVs induce more potent transgene product-specific immune responses compared to a single-stranded genomePreclinical safety of RNAi-mediated HTT suppression in the rhesus macaque as a potential therapy for Huntington's diseaseGene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administrationEngineered newcastle disease virus as an improved oncolytic agent against hepatocellular carcinomaIntelligent design: combination therapy with oncolytic virusesmiR-122 continues to blaze the trail for microRNA therapeuticsSystemic delivery of synthetic microRNA-16 inhibits the growth of metastatic prostate tumors via downregulation of multiple cell-cycle genesPotentiating cancer immunotherapy using an oncolytic virusA transposon and transposase system for human applicationZinc-finger nuclease-induced gene repair with oligodeoxynucleotides: wanted and unwanted target locus modificationsIL-28B/IFN-lambda 3 drives granzyme B loading and significantly increases CTL killing activity in macaquesLentiviral vector gene therapy: effective and safe?Comparative analysis of transposable element vector systems in human cellsMicroRNAs regulate ocular neovascularizationSystemic correction of storage disease in MPS I NOD/SCID mice using the sleeping beauty transposon systemEnhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapyEnhancement of oncolytic properties of recombinant newcastle disease virus through antagonism of cellular innate immune responsesA highly stable and nonintegrated human artificial chromosome (HAC) containing the 2.4 Mb entire human dystrophin genePCSK9 LNA antisense oligonucleotides induce sustained reduction of LDL cholesterol in nonhuman primatesBiomaterials approach to expand and direct differentiation of stem cellsErythroid-specific human factor IX delivery from in vivo selected hematopoietic stem cells following nonmyeloablative conditioning in hemophilia B miceGenome-editing Technologies for Gene and Cell TherapyNuclease Target Site Selection for Maximizing On-target Activity and Minimizing Off-target Effects in Genome EditingModulation of Protein-Protein Interactions for the Development of Novel TherapeuticsDevelopment of Novel Adenoviral Vectors to Overcome Challenges Observed With HAdV-5-based ConstructsEngineered Viruses as Genome Editing DevicesParkinson's disease gene therapy: success by design meets failure by efficacyRetroviral integrations in gene therapy trialsGenetically modified hematopoietic stem cell transplantation for HIV-1-infected patients: can we achieve a cure?
P1433
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P1433
description
journal
@en
revista científica
@es
revue scientifique
@fr
rivista scientifica
@it
wetenschappelijk tijdschrift van Elsevier
@nl
wissenschaftliche Fachzeitschrift
@de
مجلة
@ar
name
Molecular Therapy
@ast
Molecular Therapy
@da
Molecular Therapy
@en
Molecular Therapy
@es
Molecular Therapy
@fi
Molecular Therapy
@fr
Molecular Therapy
@it
Molecular Therapy
@nb
Molecular Therapy
@nl
Molecular Therapy
@nn
type
label
Molecular Therapy
@ast
Molecular Therapy
@da
Molecular Therapy
@en
Molecular Therapy
@es
Molecular Therapy
@fi
Molecular Therapy
@fr
Molecular Therapy
@it
Molecular Therapy
@nb
Molecular Therapy
@nl
Molecular Therapy
@nn
prefLabel
Molecular Therapy
@ast
Molecular Therapy
@da
Molecular Therapy
@en
Molecular Therapy
@es
Molecular Therapy
@fi
Molecular Therapy
@fr
Molecular Therapy
@it
Molecular Therapy
@nb
Molecular Therapy
@nl
Molecular Therapy
@nn
P3181
P1055
P1156
P123
P1250
P1277
P1476
Molecular Therapy
@und
P236
P3181
P571
2000-01-01T00:00:00Z