A chemical view of oligonucleotides for exon skipping and related drug applications
about
Regulation of mammalian transcription and splicing by Nuclear RNAiDuchenne Muscular Dystrophy: From Diagnosis to TherapyNanoparticle delivery of antisense oligonucleotides and their application in the exon skipping strategy for Duchenne muscular dystrophyEvaluation of 2'-Deoxy-2'-fluoro Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular DystrophyIdentification of a Peptide for Systemic Brain Delivery of a Morpholino Oligonucleotide in Mouse Models of Spinal Muscular AtrophyBi-specific splice-switching PMO oligonucleotides conjugated via a single peptide active in a mouse model of Duchenne muscular dystrophy.Parallel synthesis of cell-penetrating peptide conjugates of PMO toward exon skipping enhancement in Duchenne muscular dystrophy.Modulation of Splicing by Single-Stranded Silencing RNAs.The delivery of therapeutic oligonucleotidesPoly(ester amine) Composed of Polyethylenimine and Pluronic Enhance Delivery of Antisense Oligonucleotides In Vitro and in Dystrophic mdx Mice.Development of therapeutic splice-switching oligonucleotides.Peptide-mediated delivery: an overview of pathways for efficient internalization.Exon skipping: a first in class strategy for Duchenne muscular dystrophy.Non-coding RNAs as drug targets.Welcome to the splice age: antisense oligonucleotide-mediated exon skipping gains wider applicability.Synthesis of oligonucleotides on a soluble support.An amphipathic trans-acting phosphorothioate DNA element delivers uncharged PNA and PMO nucleic acid sequences in mammalian cellsPTP4A1 promotes TGFβ signaling and fibrosis in systemic sclerosisSolid-Phase Synthesis of Difficult Purine-Rich PNAs through Selective Hmb Incorporation: Application to the Total Synthesis of Cell Penetrating Peptide-PNAs.NRDTD: a database for clinically or experimentally supported non-coding RNAs and drug targets associations.2'β-Fluoro-Tricyclo Nucleic Acids (2'F-tc-ANA): Thermal Duplex Stability, Structural Studies, and RNase H Activation.Using Genome Sequence to Enable the Design of Medicines and Chemical Probes.An amphipathic trans-acting phosphorothioate RNA element delivers an uncharged phosphorodiamidate morpholino sequence in mdx mouse myotubes.The potential of antisense oligonucleotide therapies for inherited childhood lung diseases.Amphipathic trans-acting phosphorothioate DNA elements mediate the delivery of uncharged nucleic acid sequences in mammalian cellsCationic Oligospermine-Oligonucleotide Conjugates Provide Carrier-free Splice Switching in Monolayer Cells and Spheroids
P2860
Q26776412-FD2CE6B3-8B59-4099-894B-BD5A163A1162Q26784259-EC2C49DF-1497-45EC-BEDE-5BD3F317BF84Q26992271-7B90D362-844D-41FA-B88D-0F4BD5CDC8D0Q28831088-F3963CB5-A890-4B25-B7D6-E1D4132B7B36Q33786251-4F4D8D0A-24EE-4DAF-A181-F38DBFE8E476Q34883011-6A3A1887-AF1B-4B60-BD57-C6F94997A837Q35439476-12847280-14C5-494C-A3CA-3B7FD1671742Q35635295-67BFCD1D-16DB-428A-BABB-23AAB76AEB0EQ37210936-ADE42BBA-1A52-4AFE-8478-0E5D586AE307Q37256188-43613654-8FC8-40E2-8FAD-5BC54A65A6E1Q38211673-90C3E981-9562-47AF-8C0C-723A4F577AB1Q38285852-0088ACDA-0D3D-401D-81BB-ADE947102912Q38784820-AEAE8BF0-DD5C-4786-A0C0-6F6A160E64B5Q38904908-AB8F38B4-F7A4-48F9-989B-5B1AA179AA1EQ39617548-17338CCB-BF09-4422-B6FA-B66F012A66E3Q41147796-69E33CA7-6DEE-46E4-8598-C4250105DCA1Q42143713-8451EDF4-184D-4EB6-BFFE-B5B1BB5EDA3AQ42652598-7FDCD729-B34E-43B7-AB68-060DBA9B38BCQ43194276-6EC4D913-21B0-4C23-9E40-DD3CA5F86AD5Q47149709-343F176A-6D96-4180-BE32-51D4D45C4596Q48182856-BEC81575-E16D-4A1B-83C1-E87639E67FA5Q48263612-1649AF76-D99B-4272-AC66-43C8B1843155Q49491343-BB12CEC7-74CF-4465-A1ED-188B09E75CD1Q50146324-26C0ED39-3C48-4CFB-9AE7-3F279346E0CEQ56115525-1EA0A821-E8C0-441A-A652-D6280A0441AAQ58577275-9931289E-043C-40CD-8715-8223AE08A36D
P2860
A chemical view of oligonucleotides for exon skipping and related drug applications
description
2014 nî lūn-bûn
@nan
2014 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年学术文章
@wuu
2014年学术文章
@zh-cn
2014年学术文章
@zh-hans
2014年学术文章
@zh-my
2014年学术文章
@zh-sg
2014年學術文章
@yue
name
A chemical view of oligonucleotides for exon skipping and related drug applications
@ast
A chemical view of oligonucleotides for exon skipping and related drug applications
@en
A chemical view of oligonucleotides for exon skipping and related drug applications
@nl
type
label
A chemical view of oligonucleotides for exon skipping and related drug applications
@ast
A chemical view of oligonucleotides for exon skipping and related drug applications
@en
A chemical view of oligonucleotides for exon skipping and related drug applications
@nl
prefLabel
A chemical view of oligonucleotides for exon skipping and related drug applications
@ast
A chemical view of oligonucleotides for exon skipping and related drug applications
@en
A chemical view of oligonucleotides for exon skipping and related drug applications
@nl
P2860
P3181
P356
P1476
A chemical view of oligonucleotides for exon skipping and related drug applications
@en
P2093
Liz O'Donovan
Michael J Gait
P2860
P3181
P356
10.1089/NAT.2013.0454
P407
P50
P577
2013-10-30T00:00:00Z