Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates
about
Transposon-based screens for cancer gene discovery in mouse modelsA transposon and transposase system for human applicationComparative analysis of transposable element vector systems in human cellsThe Sleeping Beauty transposon system: a non-viral vector for gene therapyNeuroprotective therapies in glaucoma: II. Genetic nanotechnology toolsThe gene therapy journey for hemophilia: are we there yet?A new approach to gene therapy using Sleeping Beauty to genetically modify clinical-grade T cells to target CD19Rabbit models for the study of human atherosclerosis: from pathophysiological mechanisms to translational medicineUnique alterations of an ultraconserved non-coding element in the 3'UTR of ZIC2 in holoprosencephalyβ-Globin sleeping beauty transposon reduces red blood cell sickling in a patient-derived CD34(+)-based in vitro modelBreeding based remobilization of Tol2 transposon in Xenopus tropicalisGenotype-independent transmission of transgenic fluorophore protein by boar spermatozoaIn vivo screening for secreted proteins that modulate glucose handling identifies interleukin-6 family members as potent hypoglycemic agentsGermline transgenic pigs by Sleeping Beauty transposition in porcine zygotes and targeted integration in the pig genomeDifferentiation of Induced Pluripotent Stem Cells to Lentoid Bodies Expressing a Lens Cell-Specific Fluorescent ReporterThe processing of repetitive extragenic palindromes: the structure of a repetitive extragenic palindrome bound to its associated nucleaseNMR structural analysis ofSleeping Beautytransposase binding to DNARetroviral vectors and transposons for stable gene therapy: advances, current challenges and perspectivesA Broad Range of Dose Optima Achieve High-level, Long-term Gene Expression After Hydrodynamic Delivery of Sleeping Beauty Transposons Using Hyperactive SB100x TransposaseGene therapy for hemophiliaMutations in the paxillin-binding site of integrin-linked kinase (ILK) destabilize the pseudokinase domain and cause embryonic lethality in miceDriving DNA transposition by lentiviral protein transductionDNA transposon-based gene vehicles - scenes from an evolutionary driveDevelopment of transgenic cloned pig models of skin inflammation by DNA transposon-directed ectopic expression of human β1 and α2 integrinGenome-wide target profiling of piggyBac and Tol2 in HEK 293: pros and cons for gene discovery and gene therapyA hyperactive sleeping beauty transposase enhances transgenesis in zebrafish embryosDNA transposons: nature and applications in genomicsKindlin-1 controls Wnt and TGF-β availability to regulate cutaneous stem cell proliferationProkaryotic expression and purification of soluble goldfish Tgf2 transposase with transposition activity.Ultrasound-targeted hepatic delivery of factor IX in hemophiliac mice.Ultrasound directs a transposase system for durable hepatic gene delivery in miceHyperactive self-inactivating piggyBac for transposase-enhanced pronuclear microinjection transgenesis.Sleeping beauty system to redirect T-cell specificity for human applications.Human satellite cells have regenerative capacity and are genetically manipulable.Dynamics of transposable elements: towards a community ecology of the genome.Directed evolution of recombinase specificity by split gene reassemblyRecent advances in genetics of the spontaneously hypertensive rat.High-level genomic integration, epigenetic changes, and expression of sleeping beauty transgeneNovel strong tissue specific promoter for gene expression in human germ cells.Multiplexed transposon-mediated stable gene transfer in human cells
P2860
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P2860
Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates
description
2009 nî lūn-bûn
@nan
2009 թուականի Յունիսին հրատարակուած գիտական յօդուած
@hyw
2009 թվականի հունիսին հրատարակված գիտական հոդված
@hy
2009年の論文
@ja
2009年論文
@yue
2009年論文
@zh-hant
2009年論文
@zh-hk
2009年論文
@zh-mo
2009年論文
@zh-tw
2009年论文
@wuu
name
Molecular evolution of a novel ...... e gene transfer in vertebrates
@ast
Molecular evolution of a novel ...... e gene transfer in vertebrates
@en
Molecular evolution of a novel ...... e gene transfer in vertebrates
@nl
type
label
Molecular evolution of a novel ...... e gene transfer in vertebrates
@ast
Molecular evolution of a novel ...... e gene transfer in vertebrates
@en
Molecular evolution of a novel ...... e gene transfer in vertebrates
@nl
prefLabel
Molecular evolution of a novel ...... e gene transfer in vertebrates
@ast
Molecular evolution of a novel ...... e gene transfer in vertebrates
@en
Molecular evolution of a novel ...... e gene transfer in vertebrates
@nl
P2093
P2860
P3181
P356
P1433
P1476
Molecular evolution of a novel ...... e gene transfer in vertebrates
@en
P2093
Abel Acosta-Sanchez
Andrea Schmitt
Boris Jerchow
Bradley Fletcher
Conny Gysemans
Csaba Miskey
Diana Pryputniewicz
Ermira Samara-Kuko
Eyayu Belay
Janka Matrai
P2860
P2888
P304
P3181
P356
10.1038/NG.343
P407
P577
2009-06-01T00:00:00Z
P5875
P6179
1034767313