Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method.

Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method.

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http://www.wikidata.org/entity/Q30383884
Advances in gene therapy for muscular dystrophiesEmpower multiplex cell and tissue-specific CRISPR-mediated gene manipulation with self-cleaving ribozymes and tRNA.CRISPR/Cas9-Mediated Genome Editing Corrects Dystrophin Mutation in Skeletal Muscle Stem Cells in a Mouse Model of Muscle Dystrophy.Exon skipping: a first in class strategy for Duchenne muscular dystrophy.CRISPR: express delivery to any DNA address.Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy.Gene correction in patient-specific iPSCs for therapy development and disease modeling.CRISPR/Cas9 Flexes Its Muscles: In Vivo Somatic Gene Editing for Muscular DystrophyGenome Editing of Monogenic Neuromuscular Diseases: A Systematic Review.Cellular Reprogramming, Genome Editing, and Alternative CRISPR Cas9 Technologies for Precise Gene Therapy of Duchenne Muscular Dystrophy.Genome engineering: a new approach to gene therapy for neuromuscular disorders.Increased Expression of Laminin Subunit Alpha 1 Chain by dCas9-VP160.Gene Editing for Duchenne Muscular Dystrophy Using the CRISPR/Cas9 Technology: The Importance of Fine-tuning the Approach.Deletion of the GAA repeats from the human frataxin gene using the CRISPR-Cas9 system in YG8R-derived cells and mouse models of Friedreich ataxia.Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing.
P2860

Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method.

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http://www.wikidata.org/entity/Q30383884
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2016 nî lūn-bûn
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2016 թուականի Յունուարին հրատարակուած գիտական յօդուած
@hyw
2016 թվականի հունվարին հրատարակված գիտական հոդված
@hy
2016年の論文
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2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
name
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@ast
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@en
type
label
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@ast
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@en
prefLabel
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@ast
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@en
P1433
P1476
P2093
P2860
P304
P31
P356
P478
P50
P577
P5875
P698
P921
P932
P356
P1433
P1476
Efficient Restoration of the D ...... lasts Using the CinDel Method.
@en
P2093
P2860
P304
P31
P356
P478
P50
P577
P5875
P698
P921
P932