Profiling of mismatch discrimination in RNAi enabled rational design of allele-specific siRNAs.
about
Designing of highly effective complementary and mismatch siRNAs for silencing a geneTargeted delivery of mutant tolerant anti-coxsackievirus artificial microRNAs using folate conjugated bacteriophage Phi29 pRNAOligonucleotide-based strategies to combat polyglutamine diseases.An evaluation of oligonucleotide-based therapeutic strategies for polyQ diseasesTailor-made RNAi knockdown against triplet repeat disease-causing alleles.Lipid nanoparticle siRNA treatment of Ebola-virus-Makona-infected nonhuman primates.siRNA has greatly elevated mismatch tolerance at 3'-UTR sites.Argonaute protein identity and pairing geometry determine cooperativity in mammalian RNA silencing.Allele-specific siRNA knockdown as a personalized treatment strategy for vascular Ehlers-Danlos syndrome in human fibroblastsAllele-selective inhibition of trinucleotide repeat genes.siRNAs with decreased off-target effect facilitate the identification of essential genes in cancer cells.NANOG modulates stemness in human colorectal cancer.Hepatocyte-targeted RNAi therapeutics for the treatment of chronic hepatitis B virus infectionEffective Small Interfering RNA Therapy to Treat CLCN7-dependent Autosomal Dominant Osteopetrosis Type 2.Analysis of piRNA-mediated silencing of active TEs in Drosophila melanogaster suggests limits on the evolution of host genome defense.Design of siRNA Therapeutics from the Molecular ScaleDisease-causing allele-specific silencing by RNA interference.Allele-specific RNA interference rescues the long-QT syndrome phenotype in human-induced pluripotency stem cell cardiomyocytes.Research progress in allele-specific expression and its regulatory mechanisms.An efficient and high-throughput electroporation microchip applicable for siRNA delivery.Anticipating and blocking HIV-1 escape by second generation antiviral shRNAs.ASPsiRNA: A Resource of ASP-siRNAs Having Therapeutic Potential for Human Genetic Disorders and Algorithm for Prediction of Their Inhibitory Efficacy.Central role of E3 ubiquitin ligase MG53 in insulin resistance and metabolic disorders.Thermodynamic basis of selectivity in guide-target-mismatched RNA interference.Inhibition of mutant huntingtin expression by RNA duplex targeting expanded CAG repeats.A novel measurement of allele discrimination for assessment of allele-specific silencing by RNA interference.
P2860
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P2860
Profiling of mismatch discrimination in RNAi enabled rational design of allele-specific siRNAs.
description
article científic
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article scientifique
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articolo scientifico
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artigo científico
@pt
bilimsel makale
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scientific article published on December 2009
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@en
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@nl
type
label
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@en
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@nl
prefLabel
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@en
Profiling of mismatch discrimi ...... ign of allele-specific siRNAs.
@nl
P2093
P2860
P356
P1476
Profiling of mismatch discrimi ...... sign of allele-specific siRNAs
@en
P2093
Deyao Zhao
Fangfang Lai
Junmei Hong
Lihe Zhang
Renping Qiao
Tong Zhang
Xianfeng Ding
Zhenjun Yang
P2860
P304
P356
10.1093/NAR/GKP835
P407
P577
2009-12-01T00:00:00Z