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Q40261444-3DC69AA9-1FDA-4DEF-8C05-2C812CFD8159
Q40261444-3DC69AA9-1FDA-4DEF-8C05-2C812CFD8159
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Statement
http://www.wikidata.org/entity/statement/Q40261444-3DC69AA9-1FDA-4DEF-8C05-2C812CFD8159
Long-term effects of systemic gene therapy in a canine model of myotubular myopathy.
P2860
Q40261444-3DC69AA9-1FDA-4DEF-8C05-2C812CFD8159
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40261444-3DC69AA9-1FDA-4DEF-8C05-2C812CFD8159
rank
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type
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Statement
wasDerivedFrom
492dc21720516abb716aceb052d05174184a1e19
P2860
Enzyme replacement therapy rescues weakness and improves muscle pathology in mice with X-linked myotubular myopathy.