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MTNA.2016.97
MTNA.2016.97
http://dx.doi.org/10.1038/MTNA.2016.97
Transposon-mediated Generation of Cellular and Mouse Models of Splicing Mutations to Assess the Efficacy of snRNA-based Therapeutics
P356
Q39145734-D5F41719-A2FA-467C-A7DD-1C7388C0535C
P356
MTNA.2016.97
http://dx.doi.org/10.1038/MTNA.2016.97