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BLOOD-2017-04-777136
BLOOD-2017-04-777136
http://dx.doi.org/10.1182/BLOOD-2017-04-777136
Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult.
P356
Q45869832-FDA09241-18E2-484B-8FD1-CC6F2A3F92B4
P356
BLOOD-2017-04-777136
http://dx.doi.org/10.1182/BLOOD-2017-04-777136