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SCI.2016.12.01
SCI.2016.12.01
http://dx.doi.org/10.21037/SCI.2016.12.01
Increased vulnerability of photoreceptors to aberrant splicing highlight the utility of AON-based therapy for CEP290-LCA.
P356
Q41071768-C9855460-C5C2-43EE-8526-87208FBCF536
P356
SCI.2016.12.01
http://dx.doi.org/10.21037/SCI.2016.12.01