Adeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspective
about
Antibodies inside of a cell can change its outside: Can intrabodies provide a new therapeutic paradigm?Ultramicroscopy as a novel tool to unravel the tropism of AAV gene therapy vectors in the brainBarriers to inhaled gene therapy of obstructive lung diseases: A reviewThe Adeno-Associated Virus Genome Packaging Puzzle.In vivo dynamics of AAV-mediated gene delivery to sensory neurons of the trigeminal gangliaIn Silico Reconstruction of the Viral Evolutionary Lineage Yields a Potent Gene Therapy VectorDifferential myofiber-type transduction preference of adeno-associated virus serotypes 6 and 9.Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids.Host Anti-antibody Responses Following Adeno-associated Virus-mediated Delivery of Antibodies Against HIV and SIV in Rhesus MonkeysRecombinant adeno-associated virus vectors in the treatment of rare diseases.Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism.CRISPR-Cas9: a promising tool for gene editing on induced pluripotent stem cells.Recombinant Adeno-Associated Virus Vector Genomes Take the Form of Long-Lived, Transcriptionally Competent Episomes in Human Muscle.Obstacles and future of gene therapy for hemophilia.Gene therapy and peripheral nerve repair: a perspective.From phenologs to silent suppressors: Identifying potential therapeutic targets for human disease.Gene therapy approaches against cancer using in vivo and ex vivo gene transfer of interleukin-12.Recent Developments in Gene Therapy for Homozygous Familial Hypercholesterolemia.Gene Editing of Human Hematopoietic Stem and Progenitor Cells: Promise and Potential Hurdles.Methods for Optimizing CRISPR-Cas9 Genome Editing Specificity.Adeno-Associated Virus (AAV) as a Vector for Gene Therapy.Host determinants of adeno-associated viral vector entry.Adeno-Associated Virus Type 2 and Hepatocellular Carcinoma?Thermal Stability as a Determinant of AAV Serotype Identity.Gene Manipulation Strategies to Identify Molecular Regulators of Axon Regeneration in the Central Nervous System.Engineered AAVs for efficient noninvasive gene delivery to the central and peripheral nervous systems.Identification of liver-specific enhancer-promoter activity in the 3' untranslated region of the wild-type AAV2 genome.Structure-guided evolution of antigenically distinct adeno-associated virus variants for immune evasion.A Scalable and Accurate Method for Quantifying Vector Genomes of Recombinant Adeno-Associated Viruses in Crude Lysate.In Vivo Excision of HIV-1 Provirus by saCas9 and Multiplex Single-Guide RNAs in Animal Models.Integration of a CD19 CAR into the TCR Alpha Chain Locus Streamlines Production of Allogeneic Gene-Edited CAR T Cells.Viral Interplay with the Host Sumoylation System.CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector.High-accuracy biodistribution analysis of adeno-associated virus variants by double barcode sequencing.Impact of transduction towards the proliferation and migration as well as the transduction efficiency of human umbilical cord-derived late endothelial progenitor cells with nine recombinant adeno-associated virus serotypes.Adeno-associated Vector Toxicity-To Be or Not to Be?Gene Therapy with Adeno-associated Virus for Cystic Fibrosis.A Robust System for Production of Superabundant VP1 Recombinant AAV Vectors.Safety and Efficacy of AAV Retrograde Pancreatic Ductal Gene Delivery in Normal and Pancreatic Cancer Mice.Infectivity of adeno-associated virus serotypes in mouse testis
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Adeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspective
description
2015 nî lūn-bûn
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2015 թուականի Մայիսին հրատարակուած գիտական յօդուած
@hyw
2015 թվականի մայիսին հրատարակված գիտական հոդված
@hy
2015年の論文
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2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Adeno-associated virus at 50: ...... uccess--a personal perspective
@ast
Adeno-associated virus at 50: ...... uccess--a personal perspective
@en
Adeno-associated virus at 50: ...... uccess--a personal perspective
@nl
type
label
Adeno-associated virus at 50: ...... uccess--a personal perspective
@ast
Adeno-associated virus at 50: ...... uccess--a personal perspective
@en
Adeno-associated virus at 50: ...... uccess--a personal perspective
@nl
prefLabel
Adeno-associated virus at 50: ...... uccess--a personal perspective
@ast
Adeno-associated virus at 50: ...... uccess--a personal perspective
@en
Adeno-associated virus at 50: ...... uccess--a personal perspective
@nl
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P1476
Adeno-associated virus at 50: ...... uccess--a personal perspective
@en
P2093
Eric Hastie
R. Jude Samulski
P2860
P304
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P356
10.1089/HUM.2015.025
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P577
2015-05-01T00:00:00Z