Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial.
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Harnessing the Potential of Human Pluripotent Stem Cells and Gene Editing for the Treatment of Retinal Degeneration.CLINICAL PROGRESS IN INHERITED RETINAL DEGENERATIONS: GENE THERAPY CLINICAL TRIALS AND ADVANCES IN GENETIC SEQUENCING.Rod Outer Segment Development Influences AAV-Mediated Photoreceptor Transduction After Subretinal Injection.Advances in Gene Therapy for Diseases of the Eye.Gene therapy approaches for the treatment of retinal disordersMertk gene expression and photoreceptor outer segment phagocytosis by cultured rat bone marrow mesenchymal stem cells.Correction of Monogenic and Common Retinal Disorders with Gene Therapy.Long-term Characterization of Retinal Degeneration in Royal College of Surgeons Rats Using Spectral-Domain Optical Coherence TomographyInclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human RetinaTaking Stock of Retinal Gene Therapy: Looking Back and Moving Forward.The Pathway From Genes to Gene Therapy in Glaucoma: A Review of Possibilities for Using Genes as Glaucoma Drugs.Rescue of the MERTK phagocytic defect in a human iPSC disease model using translational read-through inducing drugs.Gene and cell-based therapies for inherited retinal disorders: An update.Hereditary Retinal Dystrophy.Technique of retinal gene therapy: delivery of viral vector into the subretinal space.Improving miRNA Delivery by Optimizing miRNA Expression Cassettes in Diverse Virus Vectors.A novel mutation in the dominantly inherited TOPORS gene supports haploinsufficiency as the mechanism of retinitis pigmentosa.Pattern of retinal morphological and functional decay in a light-inducible, rhodopsin mutant mouse.Optical Coherence Tomography of Retinal Degeneration in Royal College of Surgeons Rats and Its Correlation with Morphology and ElectroretinographyReprogramming towards anabolism impedes degeneration in a preclinical model of retinitis pigmentosa.Gene Therapy and Stem Cell Transplantation in Retinal Disease: The New Frontier.Simple and complex retinal dystrophies are associated with profoundly different disease networksA Novel Retinal Ganglion Cell Promoter for Utility in AAV VectorsUnraveling the mysteries of pre-mRNA splicing in the retina via stem cell technology.Neutralizing Antibodies Against Adeno-Associated Virus (AAV): Measurement and Influence on Retinal Gene Delivery.Pathogenicity of a novel missense variant associated with choroideremia and its impact on gene replacement therapy.The clinical implications of molecular monitoring and analyses of inherited retinal diseases.Gene therapy for inherited retinal and optic nerve degenerations.The pigmented epithelium, a bright partner against photoreceptor degeneration.Human Retinal Explant Culture for Ex Vivo Validation of AAV Gene Therapy.Vector Shedding and Immunogenicity Sampling for Retinal Gene Therapy.A splice-site variant in FLVCR1 produces retinitis pigmentosa without posterior column ataxia.Intravitreal, Subretinal, and Suprachoroidal Injections: Evolution of Microneedles for Drug Delivery.Synthetic adeno-associated viral vector efficiently targets mouse and non-human primate retina in vivo.CRISPR in the Retina: Evaluation of Future Potential.Assessment of the Electronic Retinal Implant Alpha AMS in Restoring Vision to Blind Patients with End-Stage Retinitis Pigmentosa.Ocular Drug Delivery.BEST1 gene therapy corrects a diffuse retina-wide microdetachment modulated by light exposure.Volumetric Measurement of Subretinal Blebs Using Microscope-Integrated Optical Coherence Tomography.Gene therapy and genome surgery in the retina.
P2860
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P2860
Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial.
description
2016 nî lūn-bûn
@nan
2016 թուականի Յունուարին հրատարակուած գիտական յօդուած
@hyw
2016 թվականի հունվարին հրատարակված գիտական հոդված
@hy
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
name
Treatment of retinitis pigment ...... r: results of a phase I trial.
@ast
Treatment of retinitis pigment ...... r: results of a phase I trial.
@en
type
label
Treatment of retinitis pigment ...... r: results of a phase I trial.
@ast
Treatment of retinitis pigment ...... r: results of a phase I trial.
@en
prefLabel
Treatment of retinitis pigment ...... r: results of a phase I trial.
@ast
Treatment of retinitis pigment ...... r: results of a phase I trial.
@en
P2093
P2860
P50
P1433
P1476
Treatment of retinitis pigment ...... r: results of a phase I trial.
@en
P2093
Abdulrahman Alhommadi
Abdulrahman Almaghamsi
Christopher Chung
David Birch
Douglas Vollrath
Emad B Abboud
Fahad Al Saikhan
Hassan Al-Dhibi
Hisham Alkuraya
Huimin Cai
P2860
P2888
P304
P356
10.1007/S00439-016-1637-Y
P577
2016-01-29T00:00:00Z
P6179
1013988172