Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences.
about
Regulatable systemic production of monoclonal antibodies by in vivo muscle electroporationDisease rescue and increased lifespan in a model of cardiomyopathy and muscular dystrophy by combined AAV treatmentsThe smooth muscle myosin heavy chain gene exhibits smooth muscle subtype-selective modular regulation in vivo.Nonviral gene transfer to skeletal, smooth, and cardiac muscle in living animalsIdentification of synthetic endothelial cell-specific promoters by use of a high-throughput screen.Development of a therapeutically important radiation induced promoter.Gene therapy by electroporation for the treatment of chronic renal failure in companion animalsPartial restoration of cardiac function with ΔPDZ nNOS in aged mdx model of Duchenne cardiomyopathy.Adeno-associated viral vectors for gene transfer and gene therapy.Computational design and application of endogenous promoters for transcriptionally targeted gene therapy for rheumatoid arthritisA comparison of the growth responses following intramuscular GHRH plasmid administration versus daily growth hormone injections in young pigsRemission of diabetes by insulin gene therapy using a hepatocyte-specific and glucose-responsive synthetic promoterTwo-step transcriptional amplification as a method for imaging reporter gene expression using weak promoters.Systemic gene transfer reveals distinctive muscle transduction profile of tyrosine mutant AAV-1, -6, and -9 in neonatal dogs.Gene therapy for Parkinson's disease: review and update.Cross signaling, cell specificity, and physiology.Identification of functional cis-regulatory elements by sequential enrichment from a randomized synthetic DNA library.Non-viral gene delivery in skeletal muscle: a protein factory.Synthetic promoter elements obtained by nucleotide sequence variation and selection for activity.Transcriptionally targeted gene therapy to detect and treat cancer.Effects of APC De-targeting and GAr modification on the duration of luciferase expression from plasmid DNA delivered to skeletal muscleSystemic protein delivery by muscle-gene transfer is limited by a local immune response.Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD).Vascular-targeted cancer gene therapy.Adiponectin gene therapy ameliorates high-fat, high-sucrose diet-induced metabolic perturbations in mice.piggyBac transposons expressing full-length human dystrophin enable genetic correction of dystrophic mesoangioblasts.Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector.Emerging vectors and targeting methods for nonviral gene therapy.Plasmid-based gene therapy of diabetes mellitus.Long-term robust myocardial transduction of the dog heart from a peripheral vein by adeno-associated virus serotype-8.Full-length Dysferlin Transfer by the Hyperactive Sleeping Beauty Transposase Restores Dysferlin-deficient Muscle.DNA vaccination and gene therapy: optimization and delivery for cancer therapy.Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy.AAV-directed muscular dystrophy gene therapy.PABPN1 gene therapy for oculopharyngeal muscular dystrophyStructure-Based Designed Nano-Dysferlin Significantly Improves Dysferlinopathy in BLA/J Mice.Cis-splicing and translation of the pre-trans-splicing molecule combine with efficiency in spliceosome-mediated RNA trans-splicingProgress toward Gene Therapy for Duchenne Muscular Dystrophy.Strength and muscle specificity of a compact promoter derived from the slow troponin I gene in the context of episomal (gutless adenovirus) and integrating (lentiviral) vectors.Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice.
P2860
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P2860
Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences.
description
1999 nî lūn-bûn
@nan
1999 թուականի Մարտին հրատարակուած գիտական յօդուած
@hyw
1999 թվականի մարտին հրատարակված գիտական հոդված
@hy
1999年の論文
@ja
1999年論文
@yue
1999年論文
@zh-hant
1999年論文
@zh-hk
1999年論文
@zh-mo
1999年論文
@zh-tw
1999年论文
@wuu
name
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@ast
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@en
type
label
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@ast
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@en
prefLabel
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@ast
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@en
P2093
P2860
P356
P1433
P1476
Synthetic muscle promoters: ac ...... ccurring regulatory sequences.
@en
P2093
E M Eastman
R Draghia-Akli
R J Schwartz
P2860
P2888
P304
P356
10.1038/6981
P577
1999-03-01T00:00:00Z