Pharmacokinetics, pharmacodynamics, and efficacy of a small-molecule SMN2 splicing modifier in mouse models of spinal muscular atrophy
about
Somatic Therapy of a Mouse SMA Model with a U7 snRNA Gene Correcting SMN2 SplicingRNA-sequencing of a mouse-model of spinal muscular atrophy reveals tissue-wide changes in splicing of U12-dependent introns.Advances in modeling and treating spinal muscular atrophyTranslational development of splice-modifying antisense oligomers.Treating pediatric neuromuscular disorders: The future is now.
P2860
Pharmacokinetics, pharmacodynamics, and efficacy of a small-molecule SMN2 splicing modifier in mouse models of spinal muscular atrophy
description
2016 nî lūn-bûn
@nan
2016 թուականի Փետրուարին հրատարակուած գիտական յօդուած
@hyw
2016 թվականի փետրվարին հրատարակված գիտական հոդված
@hy
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
name
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@ast
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@en
type
label
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@ast
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@en
prefLabel
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@ast
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@en
P2093
P2860
P921
P356
P1476
Pharmacokinetics, pharmacodyna ...... els of spinal muscular atrophy
@en
P2093
Amal Dakka
Anna Mollin
Chien-Ping Ko
Ellen M Welch
Francesco Lotti
Friedrich Metzger
Hasane Ratni
Jana Narasimhan
Janet Petruska
P2860
P304
P356
10.1093/HMG/DDW062
P577
2016-02-29T00:00:00Z