Evidence-based medicine for rare diseases: implications for data interpretation and clinical trial design.
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The National Clinical Trials Network: Conducting Successful Clinical Trials of New Therapies for Rare CancersTherapy of collagen VI-related myopathies (Bethlem and Ullrich).Rare Cancers Europe (RCE) methodological recommendations for clinical studies in rare cancers: a European consensus position paper.Uncertainty and equipoise: at interplay between epistemology, decision making and ethicsPublication bias in Kienböck's disease: systematic review.Clinical evidence for orphan medicinal products-a cause for concern?Bayesian approach to the assessment of the population-specific risk of inhibitors in hemophilia A patients: a case study.A theoretical framework for early human studies: uncertainty, intervention ensembles, and boundaries.Using a meta-narrative literature review and focus groups with key stakeholders to identify perceived challenges and solutions for generating robust evidence on the effectiveness of treatments for rare diseases.
P2860
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P2860
Evidence-based medicine for rare diseases: implications for data interpretation and clinical trial design.
description
2007 nî lūn-bûn
@nan
2007 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2007 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2007年の論文
@ja
2007年論文
@yue
2007年論文
@zh-hant
2007年論文
@zh-hk
2007年論文
@zh-mo
2007年論文
@zh-tw
2007年论文
@wuu
name
Evidence-based medicine for ra ...... ion and clinical trial design.
@ast
Evidence-based medicine for ra ...... ion and clinical trial design.
@en
type
label
Evidence-based medicine for ra ...... ion and clinical trial design.
@ast
Evidence-based medicine for ra ...... ion and clinical trial design.
@en
prefLabel
Evidence-based medicine for ra ...... ion and clinical trial design.
@ast
Evidence-based medicine for ra ...... ion and clinical trial design.
@en
P2093
P2860
P1433
P1476
Evidence-based medicine for ra ...... ion and clinical trial design.
@en
P2093
Ambuj Kumar
Heloisa P Soares
Lubomir Sokol
Madhusmita Behera
P2860
P304
P356
10.1177/107327480701400209
P577
2007-04-01T00:00:00Z